Dori, A., Scutifero, M., Passamano, L., Zoppi, D. ., Ruggiero, L., Trabacca, A. and Politano, L. (2024) “Treatment with ataluren of four symptomatic nmDMD carriers. A pilot study”, Acta Myologica. doi: 10.36185/2532-1900-398.