Dori, A., M. Scutifero, L. Passamano, D. . Zoppi, L. Ruggiero, A. Trabacca, and L. Politano. “Treatment With Ataluren of Four Symptomatic NmDMD Carriers. A Pilot Study”. Acta Myologica, Feb. 2024, doi:10.36185/2532-1900-398.