1.
Bitetti I, Manna MR, Stella R, Varone A. Sequential treatment with nusinersen, Zolgensma® and risdiplam in a paediatric patient with spinal muscular atrophytype 1: a case report. MYO [Internet]. 2023 Sep. 30 [cited 2023 Dec. 3];42(2-3). Available from: https://www.actamyologica.it/article/view/356